Our Rare Disease Experience

Canavan Disease Gene Therapy Clinical Trial

Congenital Adrenal Hyperplasia (CAH) Gene Therapy Clinical Trial

Myasthenia gravis Phase 2/3 Clinical Trial

Ornithine Transcarbamylase Deficiency (OTCD) Phase 2/3 Clinical Trial

Generalized pustular psoriasis (GPP) Real World Data

Warm antibody hemolytic anemia (wAIHA) Real World Data

DUP15q Real World Data

Myositis Real World Data

Idiopathic pulmonary fibrosis (IPF) Phase 2/3 Clinical Trial

Pouchitis Phase 2/3 Clinical Trial

Sickle Cell Digital Campaigns

Friedreich ataxia (FA) Digital Campaigns

We've Randomized Patients Across Different Countries

Our patient engagement solutions enable us to craft tailored,
omnichannel communications to support your drug
development, post-approval research, or commercialization effort.

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